Our mission and vision
We aim to give children and their families, affected by the orphan diseases, a fair access to life-changing therapies and a new hope for the future.
Our model
Hand-in-hand with patients, EspeRare rescues and repositions therapies in rare diseases, thus accelerating the development of accessible treatments for these underserved patients.
R&D programmes
EspeRare is building a diversified portfolio of programmes with strong therapeutic potential. Today, our programmes include genetic diseases affecting muscle, heart and skin.
Recent news
28Oct
EspeRare is participating in the 8th iFeTIS Annual Meeting, being represented by Agnes Jaulent, PhD, and Sebastien Mazzuri, MD. The event taking...
21Oct
Caroline Kant, Executive Director of EspeRare, will participate in the BioPharma Executive Leaders Conference in Boston on October 29, 2024. She...
Testimonials
- It is time to renovate and accelerate the discovery and development of drugs for rare diseases. Esperare is an essential player in the innovative, collaborative system that will be created to make a difference in this world.
- As a nonprofit organisation, our priorities are not determined by the size of a market, they are solely defined by the medical needs and great science. Above all, we strive to apply our patient-centric model and pharma know-how to advance new treatments for underserved patients.
- For me it is a privilege to represent Merck Serono on the Board of EspeRare, I firmly believe that this exciting new Foundation can make a real difference to the lives of patients with Duchenne Muscular Dystrophy and other rare diseases.
- Fostering access to health for patients that are the most in need is what this foundation is about, and is what I am about.
- Duchenne is a heartbreaking disease. Children like Laurent, my cousin, affected with this disease are bright and engaged but as they grow up, they inexorably get weaker and experience the loss of the few abilities they had acquired. I have in my genes the eagerness to find treatments for this disease and I am committed to give them the strength to fight their disease.